Presentations / Publications

TOPPresentations / Publications

Classification Title Presentations / Publications News
Publication Iduronate-2-sulfatase with anti-human transferrin receptor antibody for neuropathic mucopolysaccharidosis II: a phase 1/2 trial Molecular Therapy Volume 27, Issue 2, 6 February 2019, Pages 456-464
Presentation Non-clinical evaluation of a blood-brain barrier -penetrating enzyme for the treatment of Mucopolysaccharidosis I 15th Annual WORLDSymposium™ 2019, Orlando, Florida
Presentation Novel therapeutic approach for treatment of CNS manifestations in patients with Mucopolysaccharidosis 2nd Asia Pacific Lysosomal Conference,New Zealand
Presentation Current situatinon and issues for the development of allogeneic regenerative medicine -through the development of TEMCELL® HS Inj, the first allogeneic mesenchymal stem cell product in Japan- FY2019 Medical Industry Innovation Forum, Tokyo
Presentation Development of therapeutics for rare diseases using a Blood-Brain Barrier penetrating technology 139th Annual Meeting of the Pharmaceutical Society of Japan
Presentation The approach for the development of regenerative medicine in JCR pharmaceuticals -effective collaboration with Kobe Biomedical Innovation Cluster- The 18th Congress of the Japanese Society for Regenerative Medicine , Kobe
Presentation Establishment and characterization of the human transferrin receptor knock-in mouse The 66th Annual Meeting of the Japanese Association for Laboratory Animal Science, Fukuoka
Presentation 3rd Generation of electronically-controlled-injectors through the partnership between a Biopharmaceutical and an Electronics company. Prefilled syringe Seminar 2019, Tokyo
Presentation Novel enzyme replacement therapies for LSDs: challenges to address neurodegeneration The 5th International Forum of Lysosomal Disorders, Tokyo
Presentation Targeting the Central Nervous System (CNS):
ERT with BBB-penetrating Enzyme vs AAV Gene Therapy in Mouse Model of Mucopolysaccharidosis Type II
The 5th International Forum of Lysosomal Disorders, Tokyo