Presentations / Publications

TOPPresentations / Publications

Classification Title Presentations / Publications News
Publication Iduronate-2-sulfatase with anti-human transferrin receptor antibody for neuropathic mucopolysaccharidosis II: a phase 1/2 trial Molecular Therapy Volume 27, Issue 2, 6 February 2019, Pages 456-464
Presentation Non-clinical evaluation of a blood-brain barrier -penetrating enzyme for the treatment of Mucopolysaccharidosis I 15th Annual WORLDSymposium™ 2019, Orlando, Florida
2019.2.4-8
Presentation Novel therapeutic approach for treatment of CNS manifestations in patients with Mucopolysaccharidosis 2nd Asia Pacific Lysosomal Conference,New Zealand
2019.2.14-16
Presentation Current situatinon and issues for the development of allogeneic regenerative medicine -through the development of TEMCELL® HS Inj, the first allogeneic mesenchymal stem cell product in Japan- FY2019 Medical Industry Innovation Forum, Tokyo
2019.3.12
Presentation Development of therapeutics for rare diseases using a Blood-Brain Barrier penetrating technology 139th Annual Meeting of the Pharmaceutical Society of Japan
2019.3.20-23
Presentation The approach for the development of regenerative medicine in JCR pharmaceuticals -effective collaboration with Kobe Biomedical Innovation Cluster- The 18th Congress of the Japanese Society for Regenerative Medicine , Kobe
2019.3.21-23
Presentation Establishment and characterization of the human transferrin receptor knock-in mouse The 66th Annual Meeting of the Japanese Association for Laboratory Animal Science, Fukuoka
2019.5.15-17
Presentation 3rd Generation of electronically-controlled-injectors through the partnership between a Biopharmaceutical and an Electronics company. Prefilled syringe Seminar 2019, Tokyo
2019.5.22
Presentation Novel enzyme replacement therapies for LSDs: challenges to address neurodegeneration The 5th International Forum of Lysosomal Disorders, Tokyo
2019.7.11-13
Presentation Targeting the Central Nervous System (CNS):
ERT with BBB-penetrating Enzyme vs AAV Gene Therapy in Mouse Model of Mucopolysaccharidosis Type II
The 5th International Forum of Lysosomal Disorders, Tokyo
2019.7.11-13